Fluorinated Chaperone−β-Cyclodextrin Formulations for β-Glucocerebrosidase Activity Enhancement in Neuronopathic Gaucher Disease

  1. García-Moreno, M.I.
  2. De La Mata, M.
  3. Sánchez-Fernández, E.M.
  4. Benito, J.M.
  5. Díaz-Quintana, A.
  6. Fustero, S.
  7. Nanba, E.
  8. Higaki, K.
  9. Sánchez-Alcázar, J.A.
  10. García Fernández, J.M.
  11. Ortiz Mellet, C.
Journal:
Journal of Medicinal Chemistry

ISSN: 1520-4804 0022-2623

Year of publication: 2017

Volume: 60

Issue: 5

Pages: 1829-1842

Type: Article

DOI: 10.1021/ACS.JMEDCHEM.6B01550 GOOGLE SCHOLAR