A therapeutic approach to pantothenate kinase associated neurodegeneration: a pilot study

  1. Pereira, A.
  2. Fischinger Moura de Souza, C.
  3. Álvarez-Córdoba, M.
  4. Reche-López, D.
  5. Sánchez-Alcázar, J.A.
Journal:
Orphanet Journal of Rare Diseases

ISSN: 1750-1172

Year of publication: 2024

Volume: 19

Issue: 1

Type: Article

DOI: 10.1186/S13023-024-03453-X GOOGLE SCHOLAR lock_openOpen access editor