In vivo base editing of a pathogenic Eif2b5 variant improves vanishing white matter phenotypes in mice

1. Böck, D.
2. Revers, I.M.
3. Bomhof, A.S.J.
4. Hillen, A.E.J.
5. Boeijink, C.
6. Kissling, L.
7. Egli, S.
8. Moreno-Mateos, M.A.
9. van der Knaap, M.S.
10. van Til, N.P.
11. Schwank, G.