Fluorinated Chaperone−β-Cyclodextrin Formulations for β-Glucocerebrosidase Activity Enhancement in Neuronopathic Gaucher Disease
- García-Moreno, M.I.
- De La Mata, M.
- Sánchez-Fernández, E.M.
- Benito, J.M.
- Díaz-Quintana, A.
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Fustero, S.
- Nanba, E.
- Higaki, K.
- Sánchez-Alcázar, J.A.
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García Fernández, J.M.
- Ortiz Mellet, C.
Journal:
Journal of Medicinal Chemistry
ISSN: 1520-4804
Year of publication: 2017
Volume: 60
Issue: 5
Pages: 1829-1842
Type: Article